注册以创建品种、
财经事件和所关注作者内容的提醒
免费注册 已有账户? 登录
Solid Biosciences Inc是一家生命科学公司。该公司专注于开发变革性治疗,以改善Duchenne肌营养不良症(Duchenne)患者的生活。Duchenne是一种遗传性肌肉萎缩疾病,主要影响男孩。SGT-001和SGT-003是其基因转移候选产品。SGT-001和SGT-003旨在通过传递一种合成的转基因来解决Duchenne的潜在遗传原因,该转基因可产生仅在身体肌肉(包括心肌和呼吸肌)中表达的肌营养不良蛋白样蛋白。SGT-001是其主要基因转移候选基因,利用腺相关病毒(AAV)9载体。除了候选基因转移外,该公司还制定了专注于平台技术的开发计划,包括双基因表达,这项技术允许它将多个转基因包装到一个载体以及衣壳中。它正在开发SGT-001,用于通过单次静脉给药治疗Duchenne。
名称 | 年龄 | 任期 | 标题 |
---|---|---|---|
Ian F. Smith | 57 | 2020 | Executive Chair |
Adam Leo Stone | 43 | 2015 | Lead Independent Director |
Lynne Marie Sullivan | 56 | 2015 | Independent Director |
Jeffrey Chamberlain | - | 2018 | Chairman of Scientific Advisory Board |
Rajeev Shah | 46 | 2017 | Independent Director |
Ilan Ganot | 49 | 2013 | Co-founder, Strategic Advisor to the CEO & Director |
Alexander G. Cumbo | 52 | 2022 | President, CEO & Director |
Laurence A. Turka | 65 | - | Member of Scientific Advisory Board |
Michael W. Lawlor | - | - | Member of Scientific Advisory Board |
Sukumar Nagendran | 56 | 2018 | Independent Director |
Geoffrey F. Slaff | - | - | Member of Scientific Advisory Board |
Carrie Miceli | - | - | Member of Scientific Advisory Board |
Jeffrey A. Bluestone | 70 | - | Member of Scientific Advisory Board |
Clare Kahn | 71 | 2021 | Independent Director |
Martin I. Freed | 62 | 2018 | Independent Director |
Lee Sweeney | - | - | Member of Scientific Advisory Board |
Georgia Keresty | 61 | 2021 | Independent Director |
Ronald D. Cohn | - | - | Member of Scientific Advisory Board |
Dongsheng Duan | - | - | Member of Scientific Advisory Board |
Joe Kornegay | - | - | Member of the Scientific Advisory Board |
Adam M. Koppel | 54 | 2022 | Independent Director |
确定屏蔽%USER_NAME%?
如果屏蔽,您和%USER_NAME%都无法看到相互在Investing.com上发布的信息。
%USER_NAME%已成功添加至屏蔽列表
由于您刚刚取消屏蔽此人,因此必须等待48小时才能重新屏蔽。
您举报该评论的原因为:
谢谢您!
您的举报将会被发送到管理员进行审核