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Alnylam Pharmaceuticals Inc是一家商业阶段的生物制药公司。该公司的商业产品和研究性核糖核酸(RNA)干扰(RNAi)治疗剂的管线集中在四个战略治疗领域(STArs):基因药物、心脏代谢疾病、肝脏传染病和中枢神经系统/眼部疾病。该公司基于RNAi的药物包括ONPATTRO(patisiran)、GIVLAARI(givosiran)、OXLUMO(lumasiran)和Leqvio(inclisiran)。ONPATTRO是一种针对甲状腺素蛋白淀粉样变性的静脉注射RNAi治疗药物。GIVLAARI用于减少诱导的肝脏氨基乙酰丙酸合酶1mRNA,以减少与急性肝卟啉症(AHP)的发作和其他疾病表现相关的毒素。OXLUMO是一种靶向羟酸氧化酶1的RNAi疗法,用于治疗1型原发性高草酸尿症(PH1)。Leqvio用于治疗成人高胆固醇血症。
名称 | 年龄 | 任期 | 标题 |
---|---|---|---|
Yvonne L. Greenstreet | 60 | 2016 | CEO & Director |
Paul R. Schimmel | 82 | 2002 | Member of the Scientific Advisory Board |
David P. Bartel | - | - | Member of Scientific Advisory Board |
Rachel Meyers | - | - | Member of Scientific Advisory Board |
Olivier Brandicourt | 67 | 2020 | Independent Director |
Dennis Arthur Ausiello | 78 | 2012 | Member of the Scientific Advisory Board & Independent Director |
Daniel J. Rader | - | - | Member of Scientific Advisory Board |
Michael W. Bonney | 65 | 2014 | Non-Independent Director |
Nancy J. Brown | - | 2015 | Member of Scientific Advisory Board |
Margaret A. Hamburg | 68 | 2019 | Independent Director |
Carolyn R. Bertozzi | 56 | 2023 | Independent Director |
Markus Stoffel | - | - | Member of Scientific Advisory Board |
Phillip A. Sharp | 78 | 2002 | Co-Founder, Member of the Scientific Advisory Board & Independent Director |
Priya S. Kishnani | - | 2020 | Member of the Scientific Advisory Board |
Charles Elliott Sigal | 71 | 2022 | Independent Director |
David E. I. Pyott | 71 | 2015 | Independent Director |
Colleen Foley Reitan | 64 | 2018 | Independent Director |
Akshay K. Vaishnaw | 61 | 2006 | Chief Innovation Officer & Member of the Scientific Advisory Board |
Amy W. Schulman | 63 | 2014 | Independent Chair of the Board & Lead Independent Director |
Muthiah Manoharan | 71 | 2003 | Senior VP of Innovation Chemistry & Distinguished Scientist and Member of Scientific Advisory Board |
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